This is the first time such results have been achieved in both children and adult patients born with a specific type of congenital deafness.
Articles on Adeno-associated virus
Displaying all articles
Antiretroviral therapies for HIV, while extremely effective, need to be taken daily for life. Designing antibody treatments that need to be taken only once could improve compliance and reduce drug resistance.
Over 1,000 cases of severe hepatitis without any explainable cause have been reported in children so far this year.
Tay-Sachs is a rare and fatal neurodegerative disorder that most commonly affects children. Researchers have developed the first Tay-Sachs treatment to reach clinical trials.
Addiction to cocaine is wildly difficult to conquer. But physicians may soon have a new type of gene therapy for patients that makes the drug less alluring.
One big challenge for gene therapies is delivering DNA or RNA safely to cells inside patients’ bodies. New nanoparticles could be an improvement over the current standard – repurposed viruses.
Top contributors
-
Doctoral Student in Biochemistry, University of Washington
-
Associate Professor of Neurology, UMass Chan Medical School
-
Professor of Biochemistry & Cellular and Molecular Biology, University of Tennessee
-
Professor of Pathology, Vice-chair for Research, University of Miami
-
Associate Professor of Microbial Bioinformatics, Nottingham Trent University
-
Assistant Professor of Biochemistry & Cellular and Molecular Biology, University of Tennessee
-
Associate Professor, Senior Consultant, Karolinska Institutet