Down syndrome results in changes to the structure and function of neural circuits in the brain. Delivering a specific protein to neurons could reverse these changes.
Articles on AAV
Displaying all articles
Tay-Sachs is a rare and fatal neurodegerative disorder that most commonly affects children. Researchers have developed the first Tay-Sachs treatment to reach clinical trials.
Addiction to cocaine is wildly difficult to conquer. But physicians may soon have a new type of gene therapy for patients that makes the drug less alluring.
One big challenge for gene therapies is delivering DNA or RNA safely to cells inside patients’ bodies. New nanoparticles could be an improvement over the current standard – repurposed viruses.
Top contributors
-
Doctoral Student in Biochemistry, University of Washington
-
Associate Professor of Neurology, UMass Chan Medical School
-
Assistant Professor of Biochemistry & Cellular and Molecular Biology, University of Tennessee
-
Professor of Biochemistry & Cellular and Molecular Biology, University of Tennessee
-
Assistant Professor of Neuroscience, University of Virginia